Northerner
Admin (Retired)
- Relationship to Diabetes
- Type 1
A disease which robs children of the ability to walk and talk has been cured by pioneering gene therapy to correct errors in their DNA, say doctors.
The study, in the journal Science, showed the three patients were now going to school.
A second study published at the same time has shown a similar therapy reversing a severe genetic disease affecting the immune system.
Gene therapy researchers said it was a "really exciting" development.
Both diseases are caused by errors in the patient's genetic code - the manual for building and running their bodies.
http://www.bbc.co.uk/news/health-23269778
Remarkable! 🙂
The study, in the journal Science, showed the three patients were now going to school.
A second study published at the same time has shown a similar therapy reversing a severe genetic disease affecting the immune system.
Gene therapy researchers said it was a "really exciting" development.
Both diseases are caused by errors in the patient's genetic code - the manual for building and running their bodies.
http://www.bbc.co.uk/news/health-23269778
Remarkable! 🙂